There is no treatment for Duchenne muscular dystrophy. It’s a rare and fatal genetic condition that progressively weakens all muscles, including the heart. But scientists from UT Southwestern Medical Center have successfully used a gene editing tool to halt the disease in young mice.
When most little boys were running up and down stairs, Ben Dupree was using his arms to pull himself up the wood banister in his home in University Park. His mom, Debbie, knew something was wrong.